AAV9-CSA gene therapy
1 paper1 finding
- 1 lab in 1 country
- Animals1
Outcomes
1Lifespan
upin mice1
1 study
Lifespan
upin mice1
AAV9-CSA gene therapy extends lifespan in mice.
“Treatment with AAV9-CSA resulted in a significant increase in lifespan, and broad distribution of human CSA in the brain and heart.”
AnimalsCsa -/- ;Xpa -/- mouse model of Cockayne syndromeAAV9 vector encoding human CSA under a CBA promoter
AAV gene therapy for Cockayne syndrome
bioRxiv (Cold Spring Harbor Laboratory)9 Jun 2025Preprint