Mucopolysaccharidosis type VIIDisease3 papersAnimals3LatestThe Ocular Surface·12 JanSelf-complementary AAV vector therapy for treating corneal cloudiness of mucopolysaccharidosis type VII (MPS VII)Experiments in miceInterventionsPaperMolecular Therapy·19 AprGenetic correction of the fetal brain increases the lifespan of mice with the severe multisystemic disease mucopolysaccharidosis type VIIExperiments in miceInterventionsPaperBlood·1 DecIncreased life span and correction of metabolic defects in murine mucopolysaccharidosis type VII after syngeneic bone marrow transplantationExperiments in miceInterventionsPaper
The Ocular Surface·12 JanSelf-complementary AAV vector therapy for treating corneal cloudiness of mucopolysaccharidosis type VII (MPS VII)Experiments in miceInterventionsPaper
Molecular Therapy·19 AprGenetic correction of the fetal brain increases the lifespan of mice with the severe multisystemic disease mucopolysaccharidosis type VIIExperiments in miceInterventionsPaper
Blood·1 DecIncreased life span and correction of metabolic defects in murine mucopolysaccharidosis type VII after syngeneic bone marrow transplantationExperiments in miceInterventionsPaper