GA2Biomarker1 paperAnimals1LatestHuman Molecular Genetics·15 MarIntravenous administration of scAAV9-Hexb normalizes lifespan and prevents pathology in Sandhoff disease miceExperiments in miceInterventionsPaper
Human Molecular Genetics·15 MarIntravenous administration of scAAV9-Hexb normalizes lifespan and prevents pathology in Sandhoff disease miceExperiments in miceInterventionsPaper