Lafora disease
1 paper
- Human trial1
Latest
1 in 12 monthsEpileptic Disorders
Empagliflozin in Lafora disease: A first-in-human 6-month pilot study with electroclinical and FDG-PET findings
Non-randomised trial in 2 peopleEmpagliflozin
bioRxiv
Clinicopathologic Dissociation: Robust Lafora Body Accumulation in Malin KO Mice Without Observable Changes in Home-cage Behavior
Preprint: experiments in animalsMechanisms