Molecular Therapy Nucleic Acids
ADAR RNA editing for cardiovascular disease: Targeting B4GALT1 to modulate lipid metabolism through reduced galactosyltransferase activity
By Francesco De Chiara, Eva Coll-de la Rubia, Petra de Bruijn, Show 11 more authorsGerard J. Platenburg
Experiments in animalsInterventions
The paper
ProQR Therapeutics (Netherlands)
Molecular Therapy Nucleic Acids, 9 Jul 2026



