Neuropathic Gaucher diseaseDisease1 paperAnimals1LatestPLOS One·17 AugSystemic delivery of a glucosylceramide synthase inhibitor reduces CNS substrates and increases lifespan in a mouse model of type 2 Gaucher diseaseExperiments in miceInterventionsPaper
PLOS One·17 AugSystemic delivery of a glucosylceramide synthase inhibitor reduces CNS substrates and increases lifespan in a mouse model of type 2 Gaucher diseaseExperiments in miceInterventionsPaper