Autosomal dominant Emery-Dreifuss muscular dystrophyDisease1 paperAnimals1LatestScience·19 SepNeuromuscular disease. DOK7 gene therapy benefits mouse models of diseases characterized by defects in the neuromuscular junctionExperiments in miceInterventionsPaper
Science·19 SepNeuromuscular disease. DOK7 gene therapy benefits mouse models of diseases characterized by defects in the neuromuscular junctionExperiments in miceInterventionsPaper