Globoid cell leukodystrophy

1 paper

Animals1

Trial sponsors

Masonic Cancer Center, University of Minnesota
2 trialsPhase 2/3173 people

Latest

CellsApr 14

Rapamycin Alleviates Protein Aggregates, Reduces Neuroinflammation, and Rescues Demyelination in Globoid Cell Leukodystrophy

Experiments in miceRapamycin

Stem Cell ReportsMay 15

Human iPSC-based neurodevelopmental models of globoid cell leukodystrophy uncover patient- and cell type-specific disease phenotypes

Experiments in cellsMechanisms