KRRO-121
Asset
GalNAc-conjugated RNA-editing oligonucleotide targeting transcripts to correct urea cycle defects
- Stage
- Phase 1
- Modality
- Oligonucleotide
- Target
- Not known
- 2
- Indications
- 0
- Trials
- 1
- Developer
Indications
2Hepatic encephalopathy
Phase 1, globenewswire.com, 5 Oct 2026
Hyperammonemia in patients with urea cycle disorders
Phase 1, globenewswire.com, 5 Oct 2026
In the full profile
- Owner and partners1
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