Molecular Therapy
Advanced iPSC-based modeling of LMNA-related congenital muscular dystrophy enables development of genetic therapies for muscle laminopathies
By Daniel Moore, Heather B. Steele-Stallard, Luca Pinton, Show 10 more authorsFrancesco Saverio Tedesco
Experiments in cellsInterventions
The paper
The Francis Crick Institute; Great Ormond Street Hospital
Molecular Therapy, 19 Aug 2026
