Mutant huntingtin aggregate burden
Biomarker1 paper1 finding
- Animals1
Interventions
1Percept
downin mice1Very low certainty
1 study
Percept
downin mice1Very low certainty
Percept decreases mutant huntingtin aggregate burden in mice.
Animalsstriatum
Chemically modified CRISPR enzymes for multi-organ genome editing in vivo · bioRxiv : the preprint server for biology · 16 Sep 2026 · Preprint
Latest
1bioRxivAnimalsPreprint