Molecular Therapy Nucleic Acids

Cas12a chRDNA-mediated in vivo genome editing for high specificity functional gene disruption

By Marta Losa, Prachi Rajmane, Morena Stanaway, Steven Brian Kanner

Experiments in animalsInterventions

The paper

Marta Losa, Prachi Rajmane, Morena Stanaway, Steven Brian Kanner

Caribou Biosciences (United States)

Molecular Therapy Nucleic Acids, 2 Sep 2026

doi.org/10.1016/j.omtn.2026.103084 PubMed 42780917

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