Cell Reports Medicine

Targeted insertion of an optimized donor DNA is effective in a humanized mouse model of dominant retinitis pigmentosa

By Federica Esposito, Arjun Padmanabhan, Manuel Rhiel, Alberto Auricchio

Experiments in animalsInterventions

The paper

Federica Esposito, Arjun Padmanabhan, Manuel Rhiel, Alberto Auricchio

Telethon Institute Of Genetics And Medicine

Cell Reports Medicine, 11 Sep 2026

doi.org/10.1016/j.xcrm.2026.103047 PubMed 42727583

bioRxiv2 Oct 2026
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