Molecular Therapy

Multiplexed genome editing by CRISPR-Un1Cas12f1 restores dystrophin expression in a mouse model of Duchenne muscular dystrophy

By Jin-Seok Gil, Eunyoung Lee, Hyunsun Na, Taeyoung Koo

Experiments in animalsInterventions

The paper

Jin-Seok Gil, Eunyoung Lee, Hyunsun Na, Taeyoung Koo

Kyung Hee University

Molecular Therapy, 10 Sep 2026

doi.org/10.1016/j.ymthe.2026.09.006 PubMed 42723282

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