AHA Scientific Sessions 2025 Abstract

Efficacy and Safety of a Novel AAV FXN Gene Therapy (SGT-212) for the Treatment of Friedreich’s Ataxia

By Grace K. Pavlath, Jamie L. Marshall, Jun Hee Lee, Nicolas Christoforou

Experiments in animalsInterventions

The paper

Grace K. Pavlath, Jamie L. Marshall, Jun Hee Lee, Nicolas Christoforou

Solid Biosciences

AHA Scientific Sessions 2025 Abstract, 3 Nov 2025

Presented at AHA Scientific Sessions 2025, abstract 4366785

doi.org/10.1161/circ.152.suppl_3.4366785

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