Ionis Pharmaceuticals

CompanyUnited StatesFounded 1989

Wikidata

Ionis Pharmaceuticals develops one asset, in phase 1 (ION717 in prion disease). Mostly oligonucleotide acting on PRNP and proteostasis; based in the United States, founded in 1989.

1
Asset
Furthest
Phase 1
4
Trials
0
Signals

Pipeline

1
  • ION717

    Intrathecal antisense oligonucleotide reducing expression of PRNP messenger RNA to prevent prion pathology.

    Phase 1, Oligonucleotide, PRNP, Proteostasis, prion disease

Full company profiles: pipeline, trials, funding and people.

See Pro

In the full profile

  • Evidence behind the mechanisms2
  • Trials6
  • Similar companies6

Updated 9 Oct 2026 · 19 sources

Intelligence