Scn1a haploinsufficiency

Papers on Scn1a haploinsufficiency

2 papers1 new in 30 days

Thursday, October 29

Nature Biotechnology

Compact tool activates several genes at once in mice

A single virus-based delivery vehicle carried up to eight guide RNAs to activate six different genes in mice.A single virus-based delivery vehicle carried up to eight guide RNAs to activate six different genes in mice.

Mouse studyInterventions

Tuesday, March 4