bioRxiv·20 AugDelivery of small interfering RNA and antisense oligonucleotides across the blood-brain barrier with monovalent transferrin receptor 1 binding VHH-Fc fusion proteinsPreprint: experiments in animalsInterventionsPaper
AAIC 2025 Abstract·24 DecRAB5 Hyperactivation Induces APP‐Driven Endolysosomal and Autophagic Dysfunction in Down Syndrome: Reversal by Antisense Oligonucleotides Targeting App and Rab5Experiments in animalsInterventionsPaper