Lancet

Efficacy and safety of everolimus for subependymal giant cell astrocytomas associated with tuberous sclerosis complex (EXIST-1): a multicentre, randomised, placebo-controlled phase 3 trial

By Franz DN, Belousova E, Sparagana S et al.

Randomised trial in 117 peopleInterventions

Double-blind, placebo-controlled, multicentre, registered NCT00789828

The paper

Franz DN, Belousova E, Sparagana S et al.

Lancet, 14 Nov 2012

doi.org/10.1016/s0140-6736(12)61134-9PubMed 23158522